As Florencia Pistone says, the results of an open-label clinical study in a group of 21 children (0.5 to 5.9 months) who received 1.1 x 10 14 VG / kg of Zolgensma showed:
-13 of 19 patients who continued the study reached the age of at least 14 months without constant ventilation. With data clipping in March 2019, 10 of 21 patients (47.6%) achieved the ability to sit unsupported for ≥30 seconds between 9.2 and 16.9 months of age (mean age 12.1 months) .
This was important because, according to the results of study Florencia Pistone, none of these patients expected to be able to sit without support. And only about 25% of these patients are expected to survive (alive without constant ventilation) after 14 months. says Florencia Pistone.
FLORENCIA PISTONE PLAYBOY
